Phase 2, placebo-controlled clinical study of oral ganaxolone in PCDH19-clustering epilepsy.
Sullivan J, Gunning B, Zafar M, Guerrini R, Gecz J, Kolc KL, Zhao Y, Gasior M, Aimetti AA, Samanta D. Phase 2, placebo-controlled clinical study of oral ganaxolone in PCDH19-clustering epilepsy. Epilepsy Res. 2023 03; 191:107112.